Offered by: Nemours
Locations: Delaware Valley
What is the trial about?
This study will look at skin biopsies of patients with SMA to find out how certain chemicals affect cells with the SMA gene.
Who can participate?
Nemours patients with SMA of any age may participate in this study.
What is involved?
Participation will last for one visit. A skin biopsy will be taken at that visit.
Contact Nemours Clinical Trials
Trial Name: Mechanisms of Cell Death in Spinal Muscular Atrophy