Phase 2, Double-Blind, Randomized, Placebo-Controlled, Multiple Dose Study of CK-2127107


Clinical Trial

Offered by: Nemours
Location: Orlando, Fla.

Trial Name

A Phase 2, Double-Blind, Randomized, Placebo-Controlled, Multiple Dose Dtudy of CK-2127107 in Two Ascending Dose Cohorts of Patients With Spinal Muscular Atrophy (SMA).

What is the trial about?

The purpose of this study is to find out if this new drug can improve muscular weakness and fatigue for children with SMA.

Who can participate?

Children 12–18 years with SMA Type II, III or IV.

What is involved?

Seven visits to Nemours Children’s Hospital over 15 weeks. Procedures and tests to be done include physical exam, ECG, blood and urine samples, pregnancy test, various muscle tests and questions about your medical history.

Contact Nemours Clinical Trials

Trial Name: A Phase 2, Double-Blind, Randomized, Placebo-Controlled, Multiple Dose Dtudy of CK-2127107 in Two Ascending Dose Cohorts of Patients With Spinal Muscular Atrophy (SMA).

Contact Information

(800) 354-5690
ClinicalTrials@nemours.org