Offered by: Nemours Children's
Roche Drug (RO7239361) Study to Help Patients With Duchenne Muscular Dystrophy
This is a research study to find out if a new drug called RO7239361 (study drug) can help people with Duchenne Muscular Dystrophy (DMD). We also want to find out if RO7239361 is safe to take and if it is tolerated well. This drug is given by a weekly injection.
Boys, between the ages of 6 and 11 years old diagnosed with Duchenne Muscular Dystrophy.
The study involves 28 visits over the next 30 months (2.5 years). Some visits will take a couple of hours and other visits will take the full day.
Procedures include various blood draws and urine collections, ECGs, ECHOs, pulmonary function tests, endurance, grip and strength tests, questionnaires and DEXA scans.
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